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Rett Syndrome - Pipeline Review, H2 2017

Published: Oct, 2017 | Pages: 120 | Publisher: Global Markets Direct
Industry: Pharmaceuticals & Healthcare | Report Format: Electronic (PDF)

Rett Syndrome - Pipeline Review, H2 2017

Summary

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Rett Syndrome - Pipeline Review, H2 2017, provides an overview of the Rett Syndrome (Central Nervous System) pipeline landscape.

Rett syndrome is a neurodevelopmental disorder. This is caused by genetic mutation on MECP2 gene. Rett syndrome is described in four stages: Stage I or early onset, Stage II or rapid destruction, Stage III, or the plateau and Stage IV, or the late motor deterioration stage. Symptoms include slowed growth, loss of normal movement and coordination, loss of communication abilities, breathing problems, pain, irregular heartbeat and seizures. Risk factors include family history and gender. Treatment includes disease modifying drugs. 

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Rett Syndrome - Pipeline Review, H2 2017, provides comprehensive information on the therapeutics under development for Rett Syndrome (Central Nervous System), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Rett Syndrome (Central Nervous System) pipeline guide also reviews of key players involved in therapeutic development for Rett Syndrome and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase III, Phase II, Phase I, Preclinical and Discovery stages are 1, 3, 7, 7 and 2 respectively. Similarly, the Universities portfolio in Preclinical stages comprises 5 molecules, respectively.

Rett Syndrome (Central Nervous System) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct's proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

- The pipeline guide provides a snapshot of the global therapeutic landscape of Rett Syndrome (Central Nervous System).
- The pipeline guide reviews pipeline therapeutics for Rett Syndrome (Central Nervous System) by companies and universities/research institutes based on information derived from company and industry-specific sources. 
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Rett Syndrome (Central Nervous System) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Rett Syndrome (Central Nervous System) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
- The pipeline guide encapsulates all the dormant and discontinued pipeline projects. 
- The pipeline guide reviews latest news related to pipeline therapeutics for Rett Syndrome (Central Nervous System)

Reasons To Buy

- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
- Find and recognize significant and varied types of therapeutics under development for Rett Syndrome (Central Nervous System).
- Classify potential new clients or partners in the target demographic.
- Develop tactical initiatives by understanding the focus areas of leading companies.
- Plan mergers and acquisitions meritoriously by identifying key players and it's most promising pipeline therapeutics.
- Formulate corrective measures for pipeline projects by understanding Rett Syndrome (Central Nervous System) pipeline depth and focus of Indication therapeutics.
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.
 Table of Contents
Table of Contents 2 List of Tables 4 List of Figures 4 Introduction 5 Global Markets Direct Report Coverage 5 Rett Syndrome - Overview 6 Rett Syndrome - Therapeutics Development 7 Pipeline Overview 7 Pipeline by Companies 8 Pipeline by Universities/Institutes 11 Products under Development by Companies 12 Products under Development by Universities/Institutes 14 Rett Syndrome - Therapeutics Assessment 15 Assessment by Target 15 Assessment by Mechanism of Action 17 Assessment by Route of Administration 19 Assessment by Molecule Type 21 Rett Syndrome - Companies Involved in Therapeutics Development 23 AMO Pharma Ltd 23 Amorsa Therapeutics Inc 23 Anavex Life Sciences Corp 23 Apteeus 24 ArmaGen Inc 24 AveXis Inc 24 BioElectron Technology Corp 25 Biohaven Pharmaceutical Holding Company Ltd 25 Eloxx Pharmaceuticals Ltd 25 GW Pharmaceuticals Plc 26 Mitochon Pharmaceuticals Inc 26 Mitsubishi Tanabe Pharma Corp 27 Neuren Pharmaceuticals Ltd 27 Neurolixis Inc 28 Newron Pharmaceuticals SpA 28 OPKO Health Inc 28 Sage Therapeutics Inc 29 Ultragenyx Pharmaceutical Inc 29 Rett Syndrome - Drug Profiles 31 amlexanox - Drug Profile 31 AMO-04 - Drug Profile 32 ANAVEX-273 - Drug Profile 33 Antisense Oligonucleotide for Rett Syndrome - Drug Profile 43 BHV-5000 - Drug Profile 44 Bryostatin-1 - Drug Profile 45 CPT-157633 - Drug Profile 51 ELX-02 - Drug Profile 52 fingolimod hydrochloride - Drug Profile 54 Fusion Protein for Rett Syndrome - Drug Profile 61 Gene therapy to Activate MECP2 for Rett Syndrome - Drug Profile 62 Gene Therapy to Activate MECP2 for Rett Syndrome - Drug Profile 63 GWP-42006 - Drug Profile 64 LM-22A4 - Drug Profile 66 MP-101 - Drug Profile 68 NLX-101 - Drug Profile 69 SAGE-217 - Drug Profile 71 sarizotan hydrochloride - Drug Profile 75 Small Molecule to Agonize mGlu5 for Rett Syndrome - Drug Profile 78 Small Molecule to Agonize mGlu7 for Rett Syndrome - Drug Profile 79 Small Molecule to Agonize TrkB Receptor for Central Nervous System, Metabolic Disorders and ENT Disorders - Drug Profile 80 Small Molecules to Antagonize NMDA Receptor for Rett Syndrome - Drug Profile 81 trofinetide - Drug Profile 82 UX-007 - Drug Profile 90 vatiquinone - Drug Profile 97 Rett Syndrome - Dormant Projects 102 Rett Syndrome - Product Development Milestones 103 Featured News & Press Releases 103 Appendix 117 Methodology 117 Coverage 117 Secondary Research 117 Primary Research 117 Expert Panel Validation 117 Contact Us 117 Disclaimer 118
List of Tables
Number of Products under Development for Rett Syndrome, H2 2017 Number of Products under Development by Companies, H2 2017 Number of Products under Development by Companies, H2 2017 (Contd..1), H2 2017 Number of Products under Development by Universities/Institutes, H2 2017 Products under Development by Companies, H2 2017 Products under Development by Companies, H2 2017 (Contd..1), H2 2017 Products under Development by Universities/Institutes, H2 2017 Number of Products by Stage and Target, H2 2017 Number of Products by Stage and Mechanism of Action, H2 2017 Number of Products by Stage and Route of Administration, H2 2017 Number of Products by Stage and Molecule Type, H2 2017 Rett Syndrome - Pipeline by AMO Pharma Ltd, H2 2017 Rett Syndrome - Pipeline by Amorsa Therapeutics Inc, H2 2017 Rett Syndrome - Pipeline by Anavex Life Sciences Corp, H2 2017 Rett Syndrome - Pipeline by Apteeus, H2 2017 Rett Syndrome - Pipeline by ArmaGen Inc, H2 2017 Rett Syndrome - Pipeline by AveXis Inc, H2 2017 Rett Syndrome - Pipeline by BioElectron Technology Corp, H2 2017 Rett Syndrome - Pipeline by Biohaven Pharmaceutical Holding Company Ltd, H2 2017 Rett Syndrome - Pipeline by Eloxx Pharmaceuticals Ltd, H2 2017 Rett Syndrome - Pipeline by GW Pharmaceuticals Plc, H2 2017 Rett Syndrome - Pipeline by Mitochon Pharmaceuticals Inc, H2 2017 Rett Syndrome - Pipeline by Mitsubishi Tanabe Pharma Corp, H2 2017 Rett Syndrome - Pipeline by Neuren Pharmaceuticals Ltd, H2 2017 Rett Syndrome - Pipeline by Neurolixis Inc, H2 2017 Rett Syndrome - Pipeline by Newron Pharmaceuticals SpA, H2 2017 Rett Syndrome - Pipeline by OPKO Health Inc, H2 2017 Rett Syndrome - Pipeline by Sage Therapeutics Inc, H2 2017 Rett Syndrome - Pipeline by Ultragenyx Pharmaceutical Inc, H2 2017 Rett Syndrome - Dormant Projects, H2 2017



                                

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