Retinal Degeneration - Pipeline Review, H2 2014

Published: Dec, 2014 | Pages: 48 | Publisher: Global Markets Direct
Industry: Healthcare | Report Format: Electronic (PDF)

Retinal Degeneration - Pipeline Review, H2 2014

Summary

Global Markets Direct's, 'Retinal Degeneration - Pipeline Review, H2 2014', provides an overview of the Retinal Degeneration's therapeutic pipeline.

This report provides comprehensive information on the therapeutic development for Retinal Degeneration, complete with comparative analysis at various stages, therapeutics assessment by drug target, mechanism of action (MoA), route of administration (RoA) and molecule type, along with latest updates, and featured news and press releases. It also reviews key players involved in the therapeutic development for Retinal Degeneration and special features on late-stage and discontinued projects.

Global Markets Direct's report features investigational drugs from across globe covering over 20 therapy areas and nearly 3,000 indications. The report is built using data and information sourced from Global Markets Direct's proprietary databases, Company/University websites, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources, put together by Global Markets Direct's team. Drug profiles/records featured in the report undergoes periodic updation following a stringent set of processes that ensures that all the profiles are updated with the latest set of information. Additionally, processes including live news & deals tracking, browser based alert-box and clinical trials registries tracking ensure that the most recent developments are captured on a real time basis.

The report enhances decision making capabilities and help to create effective counter strategies to gain competitive advantage. It strengthens R&D pipelines by identifying new targets and MOAs to produce first-in-class and best-in-class products.

Note*: Certain sections in the report may be removed or altered based on the availability and relevance of data for the indicated disease.

Scope

- The report provides a snapshot of the global therapeutic landscape of Retinal Degeneration
- The report reviews key pipeline products under drug profile section which includes, product description, MoA and R&D brief, licensing and collaboration details & other developmental activities 
- The report reviews key players involved in the therapeutics development for Retinal Degeneration and enlists all their major and minor projects
- The report summarizes all the dormant and discontinued pipeline projects 
- A review of the Retinal Degeneration products under development by companies and universities/research institutes based on information derived from company and industry-specific sources
- Pipeline products coverage based on various stages of development ranging from pre-registration till discovery and undisclosed stages
- A detailed assessment of monotherapy and combination therapy pipeline projects
- Coverage of the Retinal Degeneration pipeline on the basis of target, MoA, route of administration and molecule type
- Latest news and deals relating related to pipeline products

Reasons to buy

- Provides strategically significant competitor information, analysis, and insights to formulate effective R&D development strategies
- Identify emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage
- Develop strategic initiatives by understanding the focus areas of leading companies
- Identify and understand important and diverse types of therapeutics under development for Retinal Degeneration
- Plan mergers and acquisitions effectively by identifying key players of the most promising pipeline
- Devise corrective measures for pipeline projects by understanding Retinal Degeneration pipeline depth and focus of Indication therapeutics
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope
- Modify the therapeutic portfolio by identifying discontinued projects and understanding the factors that drove them from pipeline

 Table of Contents
Table of Contents 2
List of Tables 4
List of Figures 5
Introduction 6
Global Markets Direct Report Coverage 6
Retinal Degeneration Overview 7
Therapeutics Development 8
Pipeline Products for Retinal Degeneration - Overview 8
Pipeline Products for Retinal Degeneration - Comparative Analysis 9
Retinal Degeneration - Therapeutics under Development by Companies 10
Retinal Degeneration - Therapeutics under Investigation by Universities/Institutes 11
Retinal Degeneration - Pipeline Products Glance 12
Clinical Stage Products 12
Early Stage Products 13
Retinal Degeneration - Products under Development by Companies 14
Retinal Degeneration - Products under Investigation by Universities/Institutes 15
Retinal Degeneration - Companies Involved in Therapeutics Development 16
AmpliPhi Biosciences Corporation 16
Aprogen, Inc. 17
BBB Therapeutics B.V. 18
GenSight Biologics 19
SanBio, Inc. 20
Senju Pharmaceutical Co., Ltd. 21
Spark Therapeutics, Inc. 22
Retinal Degeneration - Therapeutics Assessment 23
Assessment by Monotherapy Products 23
Assessment by Target 24
Assessment by Mechanism of Action 26
Assessment by Route of Administration 28
Assessment by Molecule Type 30
Drug Profiles 32
AP-202 - Drug Profile 32
Product Description 32
Mechanism of Action 32
R&D Progress 32
CB-11 - Drug Profile 33
Product Description 33
Mechanism of Action 33
R&D Progress 33
Gene Therapy for Choroideremia - Drug Profile 34
Product Description 34
Mechanism of Action 34
R&D Progress 34
Gene Therapy for Retinal Degenerative Disease - Drug Profile 35
Product Description 35
Mechanism of Action 35
R&D Progress 35
SB-623 - Drug Profile 36
Product Description 36
Mechanism of Action 36
R&D Progress 36
Small Molecule 8 for Retinitis Pigmentosa - Drug Profile 37
Product Description 37
Mechanism of Action 37
R&D Progress 37
Small Molecule to Activate NF-E2 Related Factor 2 for Central Nervous System, Metabolic Disorders, Cardiovascular and Ophthalmology - Drug Profile 38
Product Description 38
Mechanism of Action 38
R&D Progress 38
Small Molecules for Inherited Retinal Diseases - Drug Profile 39
Product Description 39
Mechanism of Action 39
R&D Progress 39
SNC-121 - Drug Profile 40
Product Description 40
Mechanism of Action 40
R&D Progress 40
SNJ-1945 - Drug Profile 41
Product Description 41
Mechanism of Action 41
R&D Progress 41
Stem Cell Therapy for Cancer, Pain, Retinal Degeneration and Niemann-Pick Disease - Drug Profile 42
Product Description 42
Mechanism of Action 42
R&D Progress 42
tgAAG-76 - Drug Profile 43
Product Description 43
Mechanism of Action 43
R&D Progress 43
Retinal Degeneration - Recent Pipeline Updates 44
Retinal Degeneration - Dormant Projects 46
Appendix 47
Methodology 47
Coverage 47
Secondary Research 47
Primary Research 47
Expert Panel Validation 47
Contact Us 48
Disclaimer 48

List of Tables
Number of Products under Development for Retinal Degeneration, H2 2014 8
Number of Products under Development for Retinal Degeneration - Comparative Analysis, H2 2014 9
Number of Products under Development by Companies, H2 2014 10
Number of Products under Investigation by Universities/Institutes, H2 2014 11
Comparative Analysis by Clinical Stage Development, H2 2014 12
Comparative Analysis by Early Stage Development, H2 2014 13
Products under Development by Companies, H2 2014 14
Products under Investigation by Universities/Institutes, H2 2014 15
Retinal Degeneration - Pipeline by AmpliPhi Biosciences Corporation, H2 2014 16
Retinal Degeneration - Pipeline by Aprogen, Inc., H2 2014 17
Retinal Degeneration - Pipeline by BBB Therapeutics B.V., H2 2014 18
Retinal Degeneration - Pipeline by GenSight Biologics, H2 2014 19
Retinal Degeneration - Pipeline by SanBio, Inc., H2 2014 20
Retinal Degeneration - Pipeline by Senju Pharmaceutical Co., Ltd., H2 2014 21
Retinal Degeneration - Pipeline by Spark Therapeutics, Inc., H2 2014 22
Assessment by Monotherapy Products, H2 2014 23
Number of Products by Stage and Target, H2 2014 25
Number of Products by Stage and Mechanism of Action, H2 2014 27
Number of Products by Stage and Route of Administration, H2 2014 29
Number of Products by Stage and Molecule Type, H2 2014 31
Retinal Degeneration Therapeutics - Recent Pipeline Updates, H2 2014 44
Retinal Degeneration - Dormant Projects, H2 2014 46