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Duchenne Muscular Dystrophy - Pipeline Review, H2 2014

Published: Jul, 2014 | Pages: 215 | Publisher: Global Markets Direct
Industry: Healthcare | Report Format: Electronic (PDF)

Duchenne Muscular Dystrophy - Pipeline Review, H2 2014

Summary

Global Markets Direct's, 'Duchenne Muscular Dystrophy - Pipeline Review, H2 2014', provides an overview of the Duchenne Muscular Dystrophy's therapeutic pipeline.

This report provides comprehensive information on the therapeutic development for Duchenne Muscular Dystrophy, complete with comparative analysis at various stages, therapeutics assessment by drug target, mechanism of action (MoA), route of administration (RoA) and molecule type, along with latest updates, and featured news and press releases. It also reviews key players involved in the therapeutic development for Duchenne Muscular Dystrophy and special features on late-stage and discontinued projects.

Global Markets Direct's report features investigational drugs from across globe covering over 20 therapy areas and nearly 3,000 indications. The report is built using data and information sourced from Global Markets Direct's proprietary databases, Company/University websites, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources, put together by Global Markets Direct's team. Drug profiles/records featured in the report undergoes periodic updation following a stringent set of processes that ensures that all the profiles are updated with the latest set of information. Additionally, processes including live news & deals tracking, browser based alert-box and clinical trials registries tracking ensure that the most recent developments are captured on a real time basis.

The report enhances decision making capabilities and help to create effective counter strategies to gain competitive advantage. It strengthens R&D pipelines by identifying new targets and MOAs to produce first-in-class and best-in-class products.

Note*: Certain sections in the report may be removed or altered based on the availability and relevance of data for the indicated disease.

Scope

- The report provides a snapshot of the global therapeutic landscape of Duchenne Muscular Dystrophy
- The report reviews key pipeline products under drug profile section which includes, product description, MoA and R&D brief, licensing and collaboration details & other developmental activities 
- The report reviews key players involved in the therapeutics development for Duchenne Muscular Dystrophy and enlists all their major and minor projects
- The report summarizes all the dormant and discontinued pipeline projects 
- A review of the Duchenne Muscular Dystrophy products under development by companies and universities/research institutes based on information derived from company and industry-specific sources
- Pipeline products coverage based on various stages of development ranging from pre-registration till discovery and undisclosed stages
- A detailed assessment of monotherapy and combination therapy pipeline projects
- Coverage of the Duchenne Muscular Dystrophy pipeline on the basis of target, MoA, route of administration and molecule type
- Latest news and deals relating related to pipeline products

Reasons to buy

- Provides strategically significant competitor information, analysis, and insights to formulate effective R&D development strategies
- Identify emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage
- Develop strategic initiatives by understanding the focus areas of leading companies
- Identify and understand important and diverse types of therapeutics under development for Duchenne Muscular Dystrophy
- Plan mergers and acquisitions effectively by identifying key players of the most promising pipeline
- Devise corrective measures for pipeline projects by understanding Duchenne Muscular Dystrophy pipeline depth and focus of Indication therapeutics
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope
- Modify the therapeutic portfolio by identifying discontinued projects and understanding the factors that drove them from pipeline
 Table of Contents
Table of Contents 2
List of Tables 5
List of Figures 6
Introduction 7
Global Markets Direct Report Coverage 7
Duchenne Muscular Dystrophy Overview 8
Therapeutics Development 9
Pipeline Products for Duchenne Muscular Dystrophy - Overview 9
Pipeline Products for Duchenne Muscular Dystrophy - Comparative Analysis 10
Duchenne Muscular Dystrophy - Therapeutics under Development by Companies 11
Duchenne Muscular Dystrophy - Therapeutics under Investigation by Universities/Institutes 15
Duchenne Muscular Dystrophy - Pipeline Products Glance 16
Late Stage Products 16
Clinical Stage Products 17
Early Stage Products 18
Duchenne Muscular Dystrophy - Products under Development by Companies 19
Duchenne Muscular Dystrophy - Products under Investigation by Universities/Institutes 23
Duchenne Muscular Dystrophy - Companies Involved in Therapeutics Development 24
Sanofi 24
Eli Lilly and Company 25
Daiichi Sankyo Company, Limited 26
Nippon Shinyaku Co., Ltd. 27
Zambon Company S.p.A. 28
Sarepta Therapeutics, Inc. 29
NicOx S.A. 30
Lexicon Pharmaceuticals, Inc. 31
Galapagos NV 32
Summit Corporation plc 33
Santhera Pharmaceuticals Holding AG 34
Shenzhen Beike Biotechnology Co., Ltd. 35
Italfarmaco S.p.A. 36
Acceleron Pharma, Inc. 37
Prosensa Holding B.V. 38
Catabasis Pharmaceuticals, Inc. 39
Nobelpharma Co., Ltd. 40
PTC Therapeutics, Inc. 41
Reata Pharmaceuticals, Inc. 42
Fate Therapeutics, Inc. 43
N-Gene Research Laboratories, Inc. 44
Asklepios BioPharmaceutical, Inc. 45
Genethon 46
miRagen Therapeutics, Inc. 47
Prosensa Therapeutics B.V. 48
Tarix Pharmaceuticals LTD. 49
EryDel SPA 50
Myomics, Inc. 51
Prothelia, Inc. 52
ReveraGen BioPharma, Inc. 53
Retrophin, LLC 54
Duchenne Muscular Dystrophy - Therapeutics Assessment 55
Assessment by Monotherapy Products 55
Assessment by Combination Products 56
Assessment by Target 57
Assessment by Mechanism of Action 61
Assessment by Route of Administration 65
Assessment by Molecule Type 67
Drug Profiles 70
ataluren - Drug Profile 70
drisapersen - Drug Profile 73
tadalafil - Drug Profile 75
idebenone - Drug Profile 77
eteplirsen - Drug Profile 80
givinostat - Drug Profile 82
PRO-045 - Drug Profile 84
CRD-007 - Drug Profile 86
halofuginone hydrobromide Delayed Release - Drug Profile 87
arbekacin - Drug Profile 89
PRO-044 - Drug Profile 90
PRO-053 - Drug Profile 92
NU-21101 + NU-21502 - Drug Profile 93
AAV1-FS-344 - Drug Profile 94
SMTC-1100 - Drug Profile 95
GLPG-0492 - Drug Profile 97
Biostrophin - Drug Profile 98
dexamethasone - Drug Profile 99
CAT-1004 - Drug Profile 101
Stem Cell Therapy for Duchenne Muscular Dystrophy - Drug Profile 103
NS-065 - Drug Profile 104
LX-2931 - Drug Profile 105
SRP-4050 - Drug Profile 107
naproxcinod - Drug Profile 108
TXA-127 - Drug Profile 110
BGP-15 - Drug Profile 112
MGN-8107 - Drug Profile 114
PRO-052 - Drug Profile 115
PRO-055 - Drug Profile 116
Gene Therapy For Duchenne Muscular Dystrophy - Drug Profile 117
Small Molecule for Duchenne Muscular Dystrophy - Drug Profile 118
PRT-01 - Drug Profile 119
PRT-20 - Drug Profile 121
VBP-15 - Drug Profile 122
RE-001 - Drug Profile 124
CAT-1040 - Drug Profile 125
poloxamer - Drug Profile 126
Small Molecule for Muscular Dystrophy and Other Muscle Disorders - Drug Profile 127
RTC-13 - Drug Profile 129
SRP-4045 - Drug Profile 131
RTC-14 - Drug Profile 132
Gene Therapy Targeting Dysferlin for Duchenne Muscular Dystrophy and Muscular Dystrophy - Drug Profile 133
Small Molecule to Activate Utrophin for Duchenne Muscular Dystrophy - Drug Profile 134
SRP-4053 - Drug Profile 135
ARM-210 - Drug Profile 136
Recombinant Protein for Muscular Dystrophy - Drug Profile 137
Gene Therapy to Activate Dystrophin for Duchenne Muscular Dystrophy - Drug Profile 138
GsMTx-4 - Drug Profile 139
Aptamer Targeting Calcineurin A for Genetic Disorders and Musculoskeletal - Drug Profile 141
Peptides for Duchenne Muscular Dystrophy and Cardiac Disease - Drug Profile 142
CAT-1041 - Drug Profile 143
MG-53 - Drug Profile 144
NBD Peptide - Drug Profile 146
SRP-4044 - Drug Profile 148
TALENs - Drug Profile 149
ACE-083 - Drug Profile 150
Small Molecules to Activate Nrf2 for Duchenne Muscular Dystrophy - Drug Profile 151
PRT-300 - Drug Profile 152
PRT-400 - Drug Profile 153
PRT-500 - Drug Profile 154
Antisense Oligonucleotide for Duchenne Muscular Dystrophy - Drug Profile 155
Small Molecules to Modulate Utrophin for Duchenne Muscular Dystrophy - Drug Profile 156
Small Molecule for Duchenne Muscular Dystrophy - Drug Profile 157
PROSPECT - Drug Profile 158
ZP-049 - Drug Profile 159
SRP-4052 - Drug Profile 160
SRP-4055 - Drug Profile 161
Next Generation Utrophin Modulator - Drug Profile 162
SRP-4008 - Drug Profile 163
Duchenne Muscular Dystrophy - Recent Pipeline Updates 164
Duchenne Muscular Dystrophy - Dormant Projects 198
Duchenne Muscular Dystrophy - Discontinued Products 199
Duchenne Muscular Dystrophy - Product Development Milestones 200
Featured News & Press Releases 200
Appendix 209
Methodology 209
Coverage 209
Secondary Research 209
Primary Research 209
Expert Panel Validation 209
Contact Us 210
Disclaimer 210
List of Tables
Number of Products under Development for Duchenne Muscular Dystrophy, H2 2014 14
Number of Products under Development for Duchenne Muscular Dystrophy - Comparative Analysis, H2 2014 15
Number of Products under Development by Companies, H2 2014 17
Number of Products under Development by Companies, H2 2014 (Contd..1) 18
Number of Products under Development by Companies, H2 2014 (Contd..2) 19
Number of Products under Investigation by Universities/Institutes, H2 2014 20
Comparative Analysis by Late Stage Development, H2 2014 21
Comparative Analysis by Clinical Stage Development, H2 2014 22
Comparative Analysis by Early Stage Development, H2 2014 23
Products under Development by Companies, H2 2014 24
Products under Development by Companies, H2 2014 (Contd..1) 25
Products under Development by Companies, H2 2014 (Contd..2) 26
Products under Development by Companies, H2 2014 (Contd..3) 27
Products under Investigation by Universities/Institutes, H2 2014 28
Duchenne Muscular Dystrophy - Pipeline by Sanofi, H2 2014 29
Duchenne Muscular Dystrophy - Pipeline by Eli Lilly and Company, H2 2014 30
Duchenne Muscular Dystrophy - Pipeline by Daiichi Sankyo Company, Limited, H2 2014 31
Duchenne Muscular Dystrophy - Pipeline by Nippon Shinyaku Co., Ltd., H2 2014 32
Duchenne Muscular Dystrophy - Pipeline by Zambon Company S.p.A., H2 2014 33
Duchenne Muscular Dystrophy - Pipeline by Sarepta Therapeutics, Inc., H2 2014 34
Duchenne Muscular Dystrophy - Pipeline by NicOx S.A., H2 2014 35
Duchenne Muscular Dystrophy - Pipeline by Lexicon Pharmaceuticals, Inc., H2 2014 36
Duchenne Muscular Dystrophy - Pipeline by Galapagos NV, H2 2014 37
Duchenne Muscular Dystrophy - Pipeline by Summit Corporation plc, H2 2014 38
Duchenne Muscular Dystrophy - Pipeline by Santhera Pharmaceuticals Holding AG, H2 2014 39
Duchenne Muscular Dystrophy - Pipeline by Shenzhen Beike Biotechnology Co., Ltd., H2 2014 40
Duchenne Muscular Dystrophy - Pipeline by Italfarmaco S.p.A., H2 2014 41
Duchenne Muscular Dystrophy - Pipeline by Acceleron Pharma, Inc., H2 2014 42
Duchenne Muscular Dystrophy - Pipeline by Prosensa Holding B.V., H2 2014 43
Duchenne Muscular Dystrophy - Pipeline by Catabasis Pharmaceuticals, Inc., H2 2014 44
Duchenne Muscular Dystrophy - Pipeline by Nobelpharma Co., Ltd., H2 2014 45
Duchenne Muscular Dystrophy - Pipeline by PTC Therapeutics, Inc., H2 2014 46
Duchenne Muscular Dystrophy - Pipeline by Reata Pharmaceuticals, Inc., H2 2014 47
Duchenne Muscular Dystrophy - Pipeline by Fate Therapeutics, Inc., H2 2014 48
Duchenne Muscular Dystrophy - Pipeline by N-Gene Research Laboratories, Inc., H2 2014 49
Duchenne Muscular Dystrophy - Pipeline by Asklepios BioPharmaceutical, Inc., H2 2014 50
Duchenne Muscular Dystrophy - Pipeline by Genethon, H2 2014 51
Duchenne Muscular Dystrophy - Pipeline by miRagen Therapeutics, Inc., H2 2014 52
Duchenne Muscular Dystrophy - Pipeline by Prosensa Therapeutics B.V., H2 2014 53
Duchenne Muscular Dystrophy - Pipeline by Tarix Pharmaceuticals LTD., H2 2014 54
Duchenne Muscular Dystrophy - Pipeline by EryDel SPA, H2 2014 55
Duchenne Muscular Dystrophy - Pipeline by Myomics, Inc., H2 2014 56
Duchenne Muscular Dystrophy - Pipeline by Prothelia, Inc., H2 2014 57
Duchenne Muscular Dystrophy - Pipeline by ReveraGen BioPharma, Inc., H2 2014 58
Duchenne Muscular Dystrophy - Pipeline by Retrophin, LLC, H2 2014 59
Assessment by Monotherapy Products, H2 2014 60
Assessment by Combination Products, H2 2014 61
Number of Products by Stage and Target, H2 2014 64
Number of Products by Stage and Mechanism of Action, H2 2014 68
Number of Products by Stage and Route of Administration, H2 2014 71
Number of Products by Stage and Molecule Type, H2 2014 74
Duchenne Muscular Dystrophy Therapeutics - Recent Pipeline Updates, H2 2014 169
Duchenne Muscular Dystrophy - Dormant Projects, H2 2014 203
Duchenne Muscular Dystrophy - Discontinued Products, H2 2014 204 



                                

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